Leucomethylthioninium API | Tau Aggregation Inhibitor API Manufacturer in India

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Leucomethylthioninium API

Leucomethylthioninium is the reduced form of methylthioninium, also known as the reduced form of methylene blue. It has been investigated as a tau aggregation inhibitor for neurodegenerative disorders, particularly Alzheimer's disease.

Leucomethylthioninium can undergo oxidation to methylthioninium and has been studied for its potential effects on abnormal tau protein aggregation, a pathological feature associated with several neurodegenerative diseases.

Leucomethylthioninium API Manufacturer in India

Leucomethylthioninium is a specialized neurodegenerative-disease research pharmaceutical ingredient requiring controlled synthesis, purification and characterization of its chemical and redox properties.

Important quality attributes include identity, assay, related substances, redox-state characterization, water content, residual solvents, elemental impurities and stability.

Chemical Information

CAS Number: 1231740-90-1
Molecular Formula: C16H18N3S+
Molecular Weight: 284.40 g/mol
Drug Class: Investigational Neurodegenerative Agent
Pharmacological Class: Tau Aggregation Inhibitor
Therapeutic Class: Neurodegenerative Disease Research Agent
Therapeutic Area: Neurology / Neurodegeneration

Mechanism of Action

Leucomethylthioninium has been investigated for its ability to interfere with tau protein aggregation.

Tau proteins can become abnormally modified and aggregate into paired helical filaments and neurofibrillary tangles in Alzheimer's disease and other tauopathies.

Research has investigated whether leucomethylthioninium-derived species can:

  • Interfere with tau aggregation
  • Reduce formation of tau filaments
  • Modulate abnormal tau protein assemblies
  • Affect pathological tau accumulation

Pharmaceutical Research Applications

Leucomethylthioninium has been investigated in research involving:

  • Alzheimer's disease
  • Tauopathies
  • Neurofibrillary tangles
  • Tau protein aggregation
  • Neurodegenerative diseases
  • Cognitive disorders
  • Neurodegenerative drug development

Its clinical-development history includes investigation as a potential disease-modifying approach targeting tau pathology.

Redox Characteristics

Leucomethylthioninium exists in a reduced redox state and can be oxidized to methylthioninium.

This redox behavior is important when evaluating:

  • Chemical identity
  • Oxidation state
  • Stability
  • Related substances
  • Conversion between reduced and oxidized forms

Therefore, appropriate analytical control of the redox state is particularly important for pharmaceutical-quality evaluation.

Manufacturing Process

Typical manufacture may involve:

  1. Preparation of the methylthioninium-related intermediate
  2. Controlled reduction
  3. Redox-state control
  4. Purification
  5. Removal of process-related impurities
  6. Crystallization or isolation
  7. Filtration
  8. Drying under controlled conditions
  9. Analytical characterization
  10. Packaging under suitable conditions

Quality and Analytical Testing

Leucomethylthioninium API quality evaluation may include:

  • Identification by HPLC
  • Mass spectrometry
  • Assay
  • Related substances
  • Redox-state determination
  • Oxidized methylthioninium content
  • Water content
  • Residual solvents
  • Elemental impurities
  • Chromatographic purity
  • Stability testing

Storage

Leucomethylthioninium should be stored under controlled pharmaceutical conditions with appropriate protection from oxygen, light, moisture and excessive heat, because its reduced redox state may be susceptible to oxidation.

Final storage conditions should be established through validated stability studies.

Pharmaceutical Research and Development

Leucomethylthioninium is relevant to research involving:

  • Tau protein
  • Tau aggregation
  • Alzheimer's disease
  • Neurofibrillary tangles
  • Tauopathies
  • Neurodegenerative disorders
  • Redox-active pharmaceutical compounds
  • Methylthioninium chemistry
  • Disease-modifying Alzheimer's research

Detailed Specifications

Parameter Specification
Appearance White to off-white crystalline powder
Identification IR & HPLC compliant
Assay (HPLC) 98.0% – 102.0%
Loss on Drying NMT 1.0%
Residue on Ignition NMT 0.5%
Individual Impurity ≤ 0.5%
Total Impurities ≤ 1.5%
Water Content NMT 1.0%
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